Oral Supplementation of Gangliosides to Treat a Rare Metabolic Disorder
NCT02234024 · Status: UNKNOWN · Phase: NA · Type: INTERVENTIONAL · Enrollment: 20
Last updated 2019-02-07
Summary
The purpose of this pilot project is to see if a supplemental form of dietary gangliosides can serve as a potential treatment for the rare metabolic condition called ganglioside GM3 synthase deficiency.
Conditions
- GM3 Synthase Deficiency
Interventions
- DIETARY_SUPPLEMENT
-
Supplementation of dairy-derived concentrated gangliosides.
Sponsors & Collaborators
-
DDC Clinic - Center for Special Needs Children
lead OTHER
Principal Investigators
-
Heng Wang, MD PhD · DDC Clinic
Study Design
- Allocation
- NA
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Max Age
- 20 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2014-01-31
- Primary Completion
- 2020-12-31
- Completion
- 2020-12-31
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