Biomarkers in Friedreich's Ataxia
NCT02497534 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 203
Last updated 2025-09-23
Summary
The purpose of this project is to characterize measures of cardiac performance and neuromuscular physiology in FA patients using novel techniques, including echocardiography and magnetic resonance imaging (MRI), metabolic exercise testing, and neurophysiological outcomes.
Conditions
Sponsors & Collaborators
-
Children's Miracle Network
collaborator OTHER -
National Institutes of Health (NIH)
collaborator NIH -
National Center for Advancing Translational Sciences (NCATS)
collaborator NIH -
University of Florida
lead OTHER
Principal Investigators
-
Manuela Corti, PT, PhD · University of Florida
Eligibility
- Min Age
- 6 Years
- Max Age
- 70 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2015-09-30
- Primary Completion
- 2030-06-03
- Completion
- 2030-06-03
Countries
- United States
Study Locations
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