The Natural History of Mucolipidosis Type IV
NCT01067742 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 7
Last updated 2026-01-26
Summary
The purpose of this study is to define the natural history of Mucolipidosis Type IV and identify potential clinical outcome measures.
Conditions
- Mucolipidosis Type IV
Sponsors & Collaborators
-
Rare Diseases Clinical Research Network
collaborator NETWORK -
National Center for Advancing Translational Sciences (NCATS)
collaborator NIH -
National Institute of Neurological Disorders and Stroke (NINDS)
collaborator NIH -
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
collaborator NIH -
Baylor Research Institute
lead OTHER
Eligibility
- Min Age
- 1 Year
- Max Age
- 64 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2009-02-19
- Primary Completion
- 2021-07-07
- Completion
- 2021-07-07
Countries
- United States
Study Locations
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