MedTrace Logo

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

NCT06747884 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 200

Last updated 2025-07-30

No results posted yet for this study

Summary

This is a natural history study to improve the types of assessments and biological samples that will be used in clinical drug trials in both congenital myotonic dystrophy and childhood myotonic dystrophy.

Conditions

  • Congenital Myotonic Dystrophy
  • Childhood Myotonic Dystrophy
  • Myotonic Dystrophy

Sponsors & Collaborators

  • National Institute of Neurological Disorders and Stroke (NINDS)

    collaborator NIH

  • SUNY Research Foundation

    collaborator OTHER

  • University of Minnesota

    collaborator OTHER

  • Roseman University of Health Sciences

    collaborator OTHER

  • University of California, San Diego

    collaborator OTHER

  • University of Glasgow

    collaborator OTHER

  • University of Kansas Medical Center

    collaborator OTHER

  • Virginia Commonwealth University

    lead OTHER

Principal Investigators

  • Nicholas Johnson, MD, MSCI, FAAN · Virginia Commonwealth University

Eligibility

Min Age
3 Years
Max Age
17 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2025-06-06
Primary Completion
2030-06-30
Completion
2030-06-30

Countries

  • United States

Study Locations

More Related Trials

Entities

Companies

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT06747884 on ClinicalTrials.gov