Optimum Insufflation Capacity in NMD
- Status
- COMPLETED
- Phase
- NA
Clinical Trials Related to Spinal Muscular Atrophy
Related studies linked through entity extraction aliases.
At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions
- Status
- COMPLETED
- Phase
- N/A
A Study to Assess the Efficacy, Safety and Pharmacokinetics of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy (SMA)
- Status
- COMPLETED
- Phase
- PHASE2
An Open-label Safety and Tolerability Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy Who Previously Participated in ISIS 396443-CS1 (NCT01494701)
- Status
- COMPLETED
- Phase
- PHASE1
Mechanisms of Cell Death in Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- N/A
An Open-label Safety, Tolerability and Dose-Range Finding Study of Multiple Doses of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Valproate and Levocarnitine in Children With Spinal Muscular Atrophy
- Status
- UNKNOWN
- Phase
- PHASE3
Short and Long Term Treatment With 4-AP in Ambulatory SMA Patients
- Status
- COMPLETED
- Phase
- PHASE2/PHASE3
Clinical Assessment of Spinal Muscular Atrophy Type II and III (SMA Europe)
- Status
- COMPLETED
- Phase
- NA
Infants With Spinal Muscular Atrophy Type I
- Status
- TERMINATED
- Phase
- N/A
Spinal Muscular Atrophy and Cardiac Autonomic Function
- Status
- COMPLETED
- Phase
- NA
An Open-label Safety, Tolerability, and Dose-range Finding Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy (SMA)
- Status
- COMPLETED
- Phase
- PHASE1
Flu Vaccine Study in Neuromuscular Patients 2011
- Status
- COMPLETED
- Phase
- PHASE4
Clinical Trial of Exercise in Patients With Spinal Muscular Atrophy (SMA)
- Status
- COMPLETED
- Phase
- NA
SMN Copy Number Distribution in Mali, West Africa
- Status
- COMPLETED
- Phase
- N/A
Evaluation of the Muscle Strength and Motor Ability in Children With Spinal Muscle Atrophy(SMA) Treated With Valproic Acid
- Status
- COMPLETED
- Phase
- N/A
Effects of Power Mobility on Young Children With Severe Motor Impairments
- Status
- COMPLETED
- Phase
- PHASE2
Motor Development and Orthoses in Spinal Muscular Atrophy (SMA)
- Status
- COMPLETED
- Phase
- N/A
A Pilot Study of Biomarkers for Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- N/A
Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular Atrophy
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2