NCT06565208 First in Human SAD/MAD Safety and PK Study With Adult DMD Safety and PK Cohort Status COMPLETED Phase EARLY_PHASE1
NCT06564974 Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT Status RECRUITING Phase N/A
NCT06540365 Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles Dystrophies Status NOT_YET_RECRUITING Phase NA
NCT06539169 FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases Status RECRUITING Phase N/A
NCT06450639 A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD) Status ACTIVE_NOT_RECRUITING Phase PHASE2
NCT06412328 Psychoeducation Program for Parents of Children with Duchenne Muscular Dystrophy Status ENROLLING_BY_INVITATION Phase NA
NCT06402942 Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy Status RECRUITING Phase NA
NCT06379906 Upper Extremity Muscle Strength, Balance and Functional Skills in DMD Status COMPLETED Phase N/A
NCT06363526 Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies. Status ENROLLING_BY_INVITATION Phase NA
NCT06328725 Evaluate the Efficacy and Safety of EN001 in Patients With Duchenne Muscular Dystrophy Status NOT_YET_RECRUITING Phase PHASE1/PHASE2
NCT06295718 Tele-assessment of Functional Performance and Quality of Life in Patients With Duchenne Muscular Dystrophy: Validity and Reliability Study Status COMPLETED Phase N/A
NCT06280209 A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy Status ACTIVE_NOT_RECRUITING Phase PHASE1/PHASE2
NCT06270719 An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy Status ENROLLING_BY_INVITATION Phase N/A