NCT00759876 Phase 2a Extension Study of Ataluren (PTC124) in Duchenne Muscular Dystrophy (DMD) Status TERMINATED Phase PHASE2
NCT00758225 Long-term Safety, Tolerability and Efficacy of Idebenone in Duchenne Muscular Dystrophy (DELPHI Extension) Status COMPLETED Phase PHASE2
NCT00606775 The Preventive Efficacy of Carvedilol on Cardiac Dysfunction in Duchenne Muscular Dystrophy Status UNKNOWN Phase PHASE4
NCT00592553 Phase 2B Study of PTC124 (Ataluren) in Duchenne/Becker Muscular Dystrophy (DMD/BMD) Status COMPLETED Phase PHASE2
NCT00468832 Longitudinal Study of the Natural History of Duchenne Muscular Dystrophy (DMD) Status UNKNOWN Phase N/A
NCT00451074 Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codons Status COMPLETED Phase PHASE1
NCT00428935 Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE1
NCT00312247 Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy Status COMPLETED Phase N/A
NCT00264888 Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE2
NCT00159250 Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE1/PHASE2
NCT00004646 Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE3