Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors
- Status
- RECRUITING
- Phase
- PHASE1/PHASE2
Clinical Trials Related to Beta-Thalassemia
Related studies linked through entity extraction aliases.
ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19
- Status
- COMPLETED
- Phase
- N/A
A Multiple Ascending Dose Study of 9MW3011 in Patients With Non-transfusion-dependent β-thalassemia
- Status
- RECRUITING
- Phase
- PHASE1
A Follow-up Study to Evaluate the Long-term Safety and Efficacy in Participants Who Received CS-101 Injection
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
A Long-term Follow-up Study in Participants Who Received CS-101
- Status
- ENROLLING_BY_INVITATION
- Phase
- N/A
Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
- Status
- RECRUITING
- Phase
- PHASE1
Adherence of Beta Thalssemia Patients to Oral Chelation Therapy
- Status
- RECRUITING
- Phase
- NA
FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases
- Status
- RECRUITING
- Phase
- N/A
Plasticizer Exposure and Its Consequences on Health
- Status
- NOT_YET_RECRUITING
- Phase
- N/A
Vitamin E Supplementation for Children With Transfusion Dependent Beta Thalassemia on Different Iron Chelation Regimen
- Status
- COMPLETED
- Phase
- NA
Long Term Beta Thalassemia Treatment: Findings From The Extension Period
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE2
A Long-term Follow-up Study in Participants Who Received CS-101
- Status
- RECRUITING
- Phase
- NA
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
- Status
- RECRUITING
- Phase
- PHASE1/PHASE2
CS-101 in Patients With β-thalassemia
- Status
- ENROLLING_BY_INVITATION
- Phase
- EARLY_PHASE1
An Open-label Study of a Gene Therapy Product (Vebeglogene Autotemcel) in Transfusion Dependent Beta-Thalassemia
- Status
- RECRUITING
- Phase
- PHASE1/PHASE2
A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Status
- RECRUITING
- Phase
- N/A
Comparison Of Efficacy And Safety Of Thalidomide Vs Hydroxyurea In Thalassemia Patients: A Single-Centre Pilot Study.
- Status
- COMPLETED
- Phase
- PHASE2
Base-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia Major
- Status
- COMPLETED
- Phase
- EARLY_PHASE1
A Clinical Study Evaluating the Safety and Efficacy of CS-101 in Treating Subjects With β-thalassemia
- Status
- COMPLETED
- Phase
- EARLY_PHASE1
Tissue Repository Providing Annotated Biospecimens for Approved Investigator-directed Biomedical Research Initiatives
- Status
- RECRUITING
- Phase
- N/A