NCT05577312 Safety and Efficacy Evaluation of BRL-101 in Subjects With Transfusion-Dependent β-Thalassemia Status ENROLLING_BY_INVITATION Phase PHASE1/PHASE2
NCT05567458 A Study to Evaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia. Status ACTIVE_NOT_RECRUITING Phase PHASE2
NCT05506358 Evaluation of Low-cost Techniques for Detecting Sickle Cell Disease and β-thalassemia in Nepal and Canada Status COMPLETED Phase NA
NCT05477563 Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease Status RECRUITING Phase PHASE3
NCT05469230 Assessment of Cognitive Function, Fatigue and Health Related Quality of Life in Children With Beta Thalassemia Status COMPLETED Phase N/A
NCT05370677 The Prevelence of IVS 1-6 (T-C) [HBB:c.92 +6 T-C] Gene Mutation in Suspected Cases of β Thalassemia in Assiut University Hospitals Status UNKNOWN Phase N/A
NCT05356195 Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT) Status ACTIVE_NOT_RECRUITING Phase PHASE3
NCT04973280 Study to Evaluate Additional Risk Minimisation Measures (aRMMs) for REBLOZYL Among Healthcare Professionals (HCPs) Status COMPLETED Phase N/A
NCT04938635 Efficacy and Safety Study of Multiple Doses of VIT-2763 in Adults With Transfusion-dependent Beta-thalassemia Status WITHDRAWN Phase PHASE2
NCT04364269 Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia Status COMPLETED Phase PHASE2
NCT04247750 Testing SIROLIMUS in Beta-thalassemia Transfusion Dependent Patients (THALA-RAP) Status UNKNOWN Phase PHASE2
NCT04208529 A Long-term Follow-up Study in Participants Who Received CTX001 Status ENROLLING_BY_INVITATION Phase PHASE3
NCT04143724 Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia Status RECRUITING Phase PHASE2
NCT04099966 AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion Status RECRUITING Phase PHASE2
NCT04064060 A Study to Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials Status RECRUITING Phase PHASE3
NCT03961828 Hyalornic Acid Level in β-Thalassemic Children Treated for Hepatitis C Virus Status COMPLETED Phase PHASE4