HALOS: A Safety, Tolerability, Pharmacokinetics and Pharmacodynamics Study of Multiple Ascending Doses of ION582 in Participants With Angelman Syndrome
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- PHASE1/PHASE2
Clinical Trials Related to Angelman Syndrome
Related studies linked through entity extraction aliases.
Angelman Syndrome Natural History Study-FAST UK
- Status
- RECRUITING
- Phase
- N/A
An Open-Label Study of the Safety, Tolerability, and Pharmacokinetics of Oral NNZ-2591 in Angelman Syndrome
- Status
- COMPLETED
- Phase
- PHASE2
A Study To Assess Distribution Of RO7248824 In The Central Nervous System Following Single Intrathecal Doses Of [89zr] Labeled RO7248824 In Healthy Male Participants
- Status
- COMPLETED
- Phase
- PHASE1
Ghrelin in Patients With a Rare Disease Associated With Intellectual Disability, and Hyperphagia, and/or Overweight, and/or Obesity
- Status
- UNKNOWN
- Phase
- N/A
Angelman Syndrome Natural History Study
- Status
- RECRUITING
- Phase
- N/A
A Study to Investigate the Safety, Tolerability, Pharmacokinetics (PK) and Pharmacodynamics (PD) of RO7248824 in Participants With Angelman Syndrome (AS)
- Status
- COMPLETED
- Phase
- PHASE1
A Study of the Safety and Tolerability of GTX-102 in Children With Angelman Syndrome
- Status
- COMPLETED
- Phase
- PHASE1/PHASE2
Angelman Syndrome (AS) Biomarker Study
- Status
- COMPLETED
- Phase
- EARLY_PHASE1
An Open-Label Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of OV101 in Individuals With Angelman Syndrome
- Status
- TERMINATED
- Phase
- PHASE3
Parent and Infant Inter(X)Action Intervention (PIXI)
- Status
- ENROLLING_BY_INVITATION
- Phase
- NA
Early Check: Expanded Screening in Newborns
- Status
- ACTIVE_NOT_RECRUITING
- Phase
- N/A
Italian Angelman Syndrome Registry
- Status
- COMPLETED
- Phase
- N/A
Nutritional Formulation for Angelman Syndrome
- Status
- COMPLETED
- Phase
- NA
Study on the Brain Network of Angelman Syndrome
- Status
- COMPLETED
- Phase
- N/A
Clinical Trial of Levodopa/Carbidopa ( Sinemet) Therapy in Angel Man Syndrome
- Status
- COMPLETED
- Phase
- NA
Single Dose Pharmacokinetic (PK) Study
- Status
- COMPLETED
- Phase
- PHASE1
A Study in Adults and Adolescents With Angelman Syndrome (STARS)
- Status
- COMPLETED
- Phase
- PHASE2
Sleep Abnormalities in Rare Genetic Disorders: AS, RTT, and PW
- Status
- COMPLETED
- Phase
- N/A
SNP-based Microdeletion and Aneuploidy RegisTry (SMART)
- Status
- COMPLETED
- Phase
- N/A