5 participants
Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type II GM1 Gangliosidosis Clinical Trial
- Study Type:
- INTERVENTIONAL
- Last Updated:
- 2026-08-31
- Start Date:
- 2027-01-01
- Completion:
- 2039-06-01
Conditions
- GM1 Gangliosidoses
- GM1 Gangliosidosis, Type I
- GM1 Gangliosidosis, Type 2
Interventions
- DRUG
No Results Yet