Clinical Trials

NCT07587242 | RECRUITING | PHASE3
70 participants

A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

Study Type:
INTERVENTIONAL
Last Updated:
2026-08-11
Start Date:
2026-08-31
Completion:
2029-05-31
Conditions
  • Muscular Dystrophies
  • Muscular Dystrophies (Duchenne, Becker, Myotonic Dystrophy)
  • Muscular Disorders, Atrophic
  • Muscular Disease
  • Musculoskeletal Diseases
  • Neuromuscular Diseases (NMD)
  • Nervous System Diseases
  • Genetic Diseases
  • X-Linked
  • Hereditary
  • Neonatal Disease
  • Duchene Muscular Dystrophy
  • Congenital
  • DMD
Interventions
  • DRUG
No Results Yet
NCT07580365 | RECRUITING | NA
22 participants

VirtualPark_Pediatric

Study Type:
INTERVENTIONAL
Last Updated:
2026-08-11
Start Date:
2026-06-30
Completion:
2026-12-31
Conditions
  • Dystrophinopathy
  • Muscular Dystrophies
  • Congenital Myopathies
Interventions
  • DEVICE
  • OTHER
No Results Yet
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