Natural History of MADD

NCT07734090 · Status: NOT_YET_RECRUITING · Type: OBSERVATIONAL · Enrollment: 50

Last updated 2026-07-29

No results posted yet for this study

Summary

The objective of this study is to conduct a longitudinal, observational investigation to determine the natural history of Multiple Acyl-CoA Dehydrogenase Deficiency (MADD), delineate the spectrum of its clinical features and their progression, identify biomarkers, and develop and validate patient reported outcomes.

Conditions

  • Multiple Acyl-CoA Dehydrogenase Deficiency

Sponsors & Collaborators

Principal Investigators

  • Mary Kate LoPiccolo, MD · Icahn School of Medicine at Mount Sinai

Eligibility

Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2026-07-31
Primary Completion
2031-07-31
Completion
2031-07-31

Countries

  • United States

Study Locations

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Entities

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT07734090 on ClinicalTrials.gov