Biomarkers for Babies and Young Children With Ataxia Telangiectasia
NCT07709728 · Status: NOT_YET_RECRUITING · Type: OBSERVATIONAL · Enrollment: 56
Last updated 2026-07-16
Summary
The goal of this observational study is to identify progressive changes of quantitative brain and lung imaging, serum and movement-related biomarkers reflecting disease progression in pre-symptomatic infants and very young children (0-5 yo) with a genetic diagnosis of A-T, that could be used in future early-life intervention trials.
Conditions
- Ataxia Telangiectasia
Sponsors & Collaborators
-
University of Nottingham
lead OTHER
Eligibility
- Min Age
- 0 Years
- Max Age
- 5 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2026-09-01
- Primary Completion
- 2029-08-31
- Completion
- 2029-08-31
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