Lysosomal Acid Lipase Deficiency in Risk Groups
NCT07455864 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 1200
Last updated 2026-05-15
Summary
A multicenter real-world observational study of the prevalence, diagnostic pathways, and clinical characteristics of lysosomal acid lipase deficiency in pediatric and adolescent risk groups in the Russian Federation (HELIOS)
Conditions
- Lysosomal Acid Lipase Deficiency
Sponsors & Collaborators
- lead INDUSTRY
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2026-02-25
- Primary Completion
- 2028-06-30
- Completion
- 2028-06-30
Countries
- Russia
Study Locations
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