Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
NCT07362875 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 75
Last updated 2026-01-23
Summary
Myotonic dystrophy (dystrophia myotonica; DM), the most prevalent form of muscular dystrophy in adults, is characterized by progressive myopathy, myotonia, and multi-systemic involvement. DM causes severe disability and profoundly affects the patient's quality of life. Currently, no effective treatments are available that alter the course of the disease, but ongoing clinical trials are underway.
Conditions
- Myotonic Dystrophy
Sponsors & Collaborators
-
Wake Forest University Health Sciences
lead OTHER
Principal Investigators
-
Araya Puwanant, MD · Wake Forest University Health Sciences
Eligibility
- Min Age
- 18 Years
- Max Age
- 65 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2025-05-15
- Primary Completion
- 2029-05-31
- Completion
- 2029-05-31
Countries
- United States
Study Locations
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