PKP2-ACM Natural History Study
NCT06644742 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 36
Last updated 2026-02-27
Summary
The goal of this study is to describe the natural history and clinical events for patients who have Arrhythmogenic Cardiomyopathy with Pathogenic Plakophilin-2 Variants (PKP2-ACM) managed with standard of care.
Conditions
- Cardiomyopathies
- Heart Diseases
- Cardiovascular Diseases
- Genetic Diseases
Sponsors & Collaborators
-
Rocket Pharmaceuticals Inc.
lead INDUSTRY
Eligibility
- Min Age
- 12 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2026-03-31
- Primary Completion
- 2030-12-31
- Completion
- 2031-04-30
Countries
- United States
- Netherlands
Study Locations
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