An Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
NCT06435000 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 75
Last updated 2025-09-19
Summary
This is an Observational Study to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
This is a multicenter study which will enroll approximately 75 subjects
Conditions
- Stargardt
- Stargardt's Disease
- Stargardt Disease
- STGD1
Sponsors & Collaborators
-
Splice Bio
lead INDUSTRY
Eligibility
- Min Age
- 12 Years
- Max Age
- 65 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2024-03-29
- Primary Completion
- 2026-12-31
- Completion
- 2027-02-28
Countries
- United States
- Germany
- United Kingdom
Study Locations
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