Study of Disease Progression in Adults With Inherited Forms of Spastic Paraplegia
NCT05008874 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 65
Last updated 2025-10-30
Summary
The course of AMN-related disabilities over time is poorly or incompletely understood due to a limited number of patients and lack of treatments. This study will help obtain a better understanding of the progression of disease with AMN and facilitate efficient clinical development of future interventional medications.
Conditions
- AMN
- AMN Gene Mutation
- X-ALD
Interventions
- OTHER
-
Natural History Observation
Data collection on progression of disease
Sponsors & Collaborators
-
SwanBio Therapeutics, Inc.
lead INDUSTRY
Eligibility
- Min Age
- 18 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2021-06-21
- Primary Completion
- 2025-05-16
- Completion
- 2025-05-16
Countries
- United States
- Germany
- Netherlands
Study Locations
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