Natural History Study of Patients With VCP-related Disease
NCT04823143 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 44
Last updated 2026-04-03
Summary
A natural history study to understand the expected progression of disease in patients with confirmed mutations in the VCP gene over 1 year.
Conditions
- IBMPFD
Sponsors & Collaborators
-
Nationwide Children's Hospital
lead OTHER
Principal Investigators
-
Lindsay Alfano · Nationwide Children's Hospital
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2021-03-18
- Primary Completion
- 2025-08-31
- Completion
- 2025-08-31
Countries
- United States
Study Locations
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