Natural History Study of Patients With Canavan Disease (CANinform Study)
NCT04126005 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 67
Last updated 2026-04-17
Summary
This study uses medical records that allow retrospective data extraction of critical milestone and motor function data. In addition, prospective assessments collect data relevant to the natural history of Canavan disease in children.
Conditions
- Canavan Disease
Sponsors & Collaborators
-
Aspa Therapeutics
lead INDUSTRY
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2019-10-10
- Primary Completion
- 2025-05-21
- Completion
- 2025-08-31
Countries
- United States
- Germany
Study Locations
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