"The MaP Study": Mapping the Patient Journey in MMA and PA
NCT03484767 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 97
Last updated 2021-08-02
Summary
Longitudinal, exploratory, natural history study of patients with MMA due to mut deficiency and PA to characterize the changes in blood disease biomarkers over time and the frequency and severity of clinical events related to their disease.
Conditions
- Methylmalonic Acidemia
- Propionic Acidemia
Sponsors & Collaborators
-
ModernaTX, Inc.
lead INDUSTRY
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2018-03-20
- Primary Completion
- 2021-05-29
- Completion
- 2021-05-29
Countries
- United States
- France
- Spain
- United Kingdom
Study Locations
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