A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype
NCT01358370 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 40
Last updated 2016-06-27
Summary
This is a Natural History study to characterize key aspects of the clinical course of lysosomal acid lipase (LAL) deficiency/Wolman phenotype in patients.
Conditions
- Lysosomal Acid Lipase Deficiency
- Wolman Disease
Sponsors & Collaborators
-
Alexion Pharmaceuticals, Inc.
lead INDUSTRY
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2010-11-30
- Primary Completion
- 2013-01-31
- Completion
- 2013-03-31
Countries
- United States
- Canada
- France
- Italy
- United Kingdom
Study Locations
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