Study of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease
NCT03201627 · Status: UNKNOWN · Phase: EARLY_PHASE1 · Type: INTERVENTIONAL · Enrollment: 18
Last updated 2019-09-24
Summary
This study is planned to study whether lithium carbonate has protective effect on the brain of Niemann-Pick disease type C1.
Conditions
- Niemann-Pick Disease, Type C1
Interventions
- DRUG
-
Lithium Carbonate
To observe whether lithium carbonate has protective role on the brain of Niemann-Pick disease C1
Sponsors & Collaborators
-
Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
lead OTHER
Study Design
- Allocation
- NON_RANDOMIZED
- Purpose
- TREATMENT
- Masking
- NONE
- Model
- SINGLE_GROUP
Eligibility
- Min Age
- 7 Years
- Max Age
- 40 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2017-07-05
- Primary Completion
- 2020-09-30
- Completion
- 2021-06-30
Countries
- China
Study Locations
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