Trehalose in Subjects With Neuronal Ceroid Lipofuscinoses
NCT04808297 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 8
Last updated 2022-04-11
Summary
Neuronal Ceroid Lipofuscinoses (NCL) or Batten's disease are the most common juvenile neurodegenerative disease, characterized by early blindness, movement disorders, cognitive and behavioral impairment, epilepsy, and retinopathy.
This study aims to collect clinical and laboratory data of patients with NCL taking Trehalose.
Conditions
- Neuronal Ceroid-Lipofuscinoses
Sponsors & Collaborators
-
IRCCS Fondazione Stella Maris
lead OTHER
Eligibility
- Min Age
- 7 Years
- Max Age
- 45 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2020-08-01
- Primary Completion
- 2021-07-01
- Completion
- 2021-10-01
Countries
- Italy
Study Locations
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