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New Imaging Technology to Assess Effect of Enzyme Replacment Therapy on Eye Disease Progession in Mucopolysacchardiosis

NCT02583152 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 50

Last updated 2017-11-28

No results posted yet for this study

Summary

Mucopolysaccharidoses (MPS) are currently treated with Enzyme replacement therapy and Bone Marrow Transplantation (BMT). No current evidence on the effectiveness on these therapies on the eye in this systemic disease is avalible. Using new imaging techniques; previously subjective data can be quantified and compared to determine if there is an improvment in the vision of patients with MPS.

Conditions

  • Mucopolysaccharidoses

Sponsors & Collaborators

Principal Investigators

  • Jane Ashworth, MBChB, PhD · Central Manchester Foundation Trust

Eligibility

Min Age
3 Years
Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2015-11-30
Primary Completion
2020-11-30
Completion
2020-11-30

Countries

  • United Kingdom

Study Locations

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Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT02583152 on ClinicalTrials.gov