A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
NCT00787995 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 353
Last updated 2014-12-08
Summary
This multicenter, multinational, longitudinal study will quantify endurance and respiratory function in subjects diagnosed with MPS IVA and will better characterize the spectrum of symptoms and biochemical abnormalities in MPS IVA disease over time.
Conditions
- MPS IV A
- Mucopolysaccharidosis IVA
- Morquio A Syndrome
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Celeste Decker, MD · BioMarin Pharmaceutical
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2008-10-31
- Primary Completion
- 2014-07-31
- Completion
- 2014-07-31
Countries
- United States
- Argentina
- Brazil
- Canada
- France
- Germany
- Italy
- Netherlands
- Taiwan
- United Kingdom
Study Locations
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