A Study to Improve the Awareness of Mucopolysaccharidosis Type II in Brazil
NCT05155488 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 250
Last updated 2022-05-09
Summary
The main aims of the study are to learn about the percentage of mucopolysaccharidosis type II (MPS II) in adults in Brazil as well as about the diagnosis process. No study medicines will be provided to participants in this study. The data available for participants diagnosed with MPS II in DATASUS (a database of the Informatics Department of Brazilian Health System) will be reviewed. No clinic visits will be required as part of participation in this study.
Conditions
- Mucopolysaccharidosis (MPS)
Interventions
- OTHER
-
No Intervention
This is a non-interventional study.
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Study Director · Takeda
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2021-12-06
- Primary Completion
- 2022-02-15
- Completion
- 2022-02-15
Countries
- Brazil
Study Locations
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