Duchenne Muscular Dystrophy Tissue Bank for Exon Skipping
NCT01772043 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 53
Last updated 2015-07-28
Summary
We will utilize the Cooperative International Neuromuscular Research Group (CINRG) network to collect and store tissue and blood from patients with Duchenne muscular dystrophy (DMD) with specific genetic mutations within the dystrophin gene that could be treated by antisense oligonucleotide (AO) drugs.
Conditions
Sponsors & Collaborators
-
Cooperative International Neuromuscular Research Group
lead NETWORK
Eligibility
- Min Age
- 4 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2012-09-30
- Primary Completion
- 2016-08-31
- Completion
- 2016-08-31
Countries
- United States
- Canada
Study Locations
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