Cystic Fibrosis Related Bone Disease: the Role of CFTR
NCT01549314 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 79
Last updated 2020-04-01
Summary
The purpose of this study is to determine whether ivacaftor, a recently FDA-approved CFTR potentiator, improves bone micro-architecture and strength in patients with cystic fibrosis with at least one G551D CFTR mutation.
Conditions
- Cystic Fibrosis Related Bone Disease
Sponsors & Collaborators
- collaborator OTHER
-
Massachusetts General Hospital
lead OTHER
Principal Investigators
-
Joel Finkelstein, MD · Massachusetts General Hospital
Eligibility
- Min Age
- 6 Years
- Max Age
- 75 Years
- Sex
- ALL
- Healthy Volunteers
- Yes
Timeline & Regulatory
- Start
- 2012-04-30
- Primary Completion
- 2018-05-31
- Completion
- 2020-02-29
Countries
- United States
Study Locations
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