The Natural History of Alpha-Mannosidosis
NCT00498420 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 45
Last updated 2020-08-03
Summary
The natural history study of the rare lysosomal disease alpha-mannosidosis will answer the question; why the rare disease develops as it does?
Conditions
- Alpha Mannosidosis
Sponsors & Collaborators
- collaborator OTHER
-
Zymenex A/S
lead INDUSTRY
Principal Investigators
-
Michael Beck, MD · Children's Hospital, University of Mainz
-
Ed Wraith, MD · Willink Biochemical Genetics Unit, Royal Manchester Childern's Hospital
-
Jiri Zeman, MD · Department of Pediatrics, Charles University
-
Dag Malm, MD · Department of Medicine, University of Tromsoe
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2007-05-31
- Primary Completion
- 2009-09-30
- Completion
- 2009-11-30
Countries
- Czechia
- Germany
- Norway
- United Kingdom
Study Locations
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