Expanded Access to Velmanase Alfa
NCT04959240 · Status: AVAILABLE · Type: EXPANDED_ACCESS
Last updated 2023-09-25
Summary
Individual patient expanded access requests may be considered for patients who have no other treatment options.
Conditions
- Alpha-Mannosidosis
Interventions
- DRUG
-
Velmanase Alfa
Sponsors & Collaborators
-
Chiesi Farmaceutici S.p.A.
lead INDUSTRY
Eligibility
- Sex
- Healthy Volunteers
- No
Timeline & Regulatory
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