A Study of Darbepoetin Alfa in Anemic Subjects With Low Risk Myelodysplastic Syndrome

Safety and Efficacy Trial of Danazol in Patients With Fanconi Anemia or Dyskeratosis Congenita

NCT01001598 ·Status: TERMINATED ·Phase: PHASE1/PHASE2

ß-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human ß-Globin Gene

NCT01639690 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

NCT01362595 ·Status: COMPLETED ·Phase: PHASE1/PHASE2

AB1 in Adult Patients with Sickle Cell Disease (SCD)

NCT05261711 ·Status: TERMINATED ·Phase: PHASE1/PHASE2

A Study of the Absorption, Metabolism, and Excretion of GBT440 in Healthy Male Subjects

NCT02497924 ·Status: COMPLETED ·Phase: PHASE1

The Efficacy and Safety of Rilzabrutinib in Participants Aged 10 to 65 Years With Sickle-cell Disease

NCT06975865 ·Status: RECRUITING ·Phase: PHASE3

A Study to Evaluate GBT021601-012 Single Dose and Multiple Dose in Participants With Sickle Cell Disease (SCD)

NCT04983264 ·Status: COMPLETED ·Phase: PHASE1

Pharmacokinetics, Pharmacodynamics and Safety of Epeleuton in Patients With Sickle Cell Disease

NCT05861453 ·Status: COMPLETED ·Phase: PHASE2

Vitamin D and Bisphosphonates in the Treatment of Sickle Cell Disease

NCT02972138 ·Status: COMPLETED

A Phase 3 Open Label Extension Study of Fostamatinib Disodium in the Treatment of Warm Antibody Autoimmune Hemolytic Anemia

NCT04138927 ·Status: ENROLLING_BY_INVITATION ·Phase: PHASE3

Study of Deferasirox for Treatment of Transfusional Iron Overload in Myelodysplastic Patients

NCT00110266 ·Status: COMPLETED ·Phase: PHASE2

Phase II Study of Arginine Butyrate With or Without Epoetin Alfa in Patients With Thalassemia Intermedia

NCT00006136 ·Status: COMPLETED ·Phase: PHASE2

EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)

NCT05444894 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1/PHASE2

A Study to Evaluate Safety, Pharmacokinetic, and Biological Activity of INCB059872 in Subjects With Sickle Cell Disease

NCT03132324 ·Status: TERMINATED ·Phase: PHASE1

Identification of Mechanism in the Erythroid Response in Patients With Myelodysplasia Undergoing Chelation Therapy

NCT01956799 ·Status: COMPLETED

Treatment of Refractory Diamond-Blackfan Anemia With Eltrombopag

NCT04269889 ·Status: COMPLETED ·Phase: PHASE1/PHASE2

Iron Overload and Transient Elastography in Patients With Myelodysplastic Syndrome

NCT02262312 ·Status: COMPLETED

Evaluating the Safety and Effectiveness of Decitabine in People With Thalassemia Intermedia

NCT00661726 ·Status: COMPLETED ·Phase: PHASE2

Study to Evaluate Darbepoetin Alfa in Pediatric Subjects With Anemia Due to Chronic Kidney Disease

NCT01428154 ·Status: WITHDRAWN ·Phase: PHASE1

A Study Evaluating the Safety and Efficacy of the BD211 Drug Product in β-Thalassemia Major Participants

NCT05015920 ·Status: COMPLETED ·Phase: NA

Gene Transfer for Sickle Cell Disease

NCT03282656 ·Status: ACTIVE_NOT_RECRUITING ·Phase: PHASE1

Haploidentical Bone Marrow Transplantation in Sickle Cell Patients (BMTCTN1507)

NCT03263559 ·Status: COMPLETED ·Phase: PHASE2

Early and Low Dose Deferasirox (3.5 mg/kg FCT) to Suppress NTBI and LPI as Early Intervention to Prevent Tissue Iron Overload in Lower Risk MDS

NCT03920657 ·Status: TERMINATED ·Phase: PHASE2

Treatment of Sickle Cell Patients Hospitalized in Pain Crisis With Prophylactic Dose Low-molecular-weight Heparin (LMWH) Versus Placebo

NCT01419977 ·Status: COMPLETED ·Phase: PHASE2

A Study of Bomedemstat (IMG-7289/MK-3543) in Participants With Polycythemia Vera (IMG-7289-CTP-203/MK-3543-004)

NCT05558696 ·Status: COMPLETED ·Phase: PHASE2