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NCT03329365 Paroxysmal Nocturnal Hemoglobinuria in ESUS & ETUS Status ACTIVE_NOT_RECRUITING Phase N/A
NCT03181633 A Long-Term Treatment Study of ACH-0144471 in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Status COMPLETED Phase PHASE2
NCT03047746 Unrelated And Partially Matched Related Donor PSCT w/ T Cell Receptor (TCR) αβ Depletion for Patients With BMF Status ACTIVE_NOT_RECRUITING Phase NA
NCT02605993 Open-label, Multiple Ascending Dose Study of Ravulizumab (ALXN1210) in Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH) Status COMPLETED Phase PHASE2
NCT02588833 Pilot Study to Assess Safety, Preliminary Efficacy and Pharmacokinetics of S.C. Pegcetacoplan (APL-2) in PNH Subjects. Status COMPLETED Phase PHASE1
NCT02534909 Proof of Concept Study to Assess the Efficacy, Safety and Pharmacokinetics of LFG316 in Patients With Paroxysmal Nocturnal Hemoglobinuria Status COMPLETED Phase PHASE2
NCT02179359 Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies Status TERMINATED Phase NA
NCT01760096 Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Subclinical Paroxysmal Nocturnal Hemoglobinuria and PNH in the Setting of Another Bone Marrow Failure Syndromes(PNH-2013) Status UNKNOWN Phase PHASE2
NCT01642979 Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Classic Paroxysmal Nocturnal Hemoglobinuria Status UNKNOWN Phase PHASE2
NCT01529827 Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic Malignancies Status COMPLETED Phase PHASE2
NCT01412047 Paroxysmal Nocturnal Hemoglobinuria Human Anti-Human Antibodies Study Status COMPLETED Phase N/A
NCT01294891 Microvascular and Cardiac Dysfunction in Paroxysmal Nocturnal Hemoglobinuria and Sickle Cell Disease Status COMPLETED Phase N/A
NCT01194804 E07-001: Safety and Efficacy Extension Study of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria Patients Status COMPLETED Phase PHASE2
NCT01192399 Safety and Efficacy Study of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria Patients Status COMPLETED Phase PHASE2
NCT00856388 Fludarabine Phosphate, Melphalan, Total-Body Irradiation, Donor Stem Cell Transplant in Treating Patients With Hematologic Cancer or Bone Marrow Failure Disorders Status COMPLETED Phase NA
NCT00731328 Donor Stem Cell Transplant After Busulfan, Fludarabine, Methylprednisolone, and Antithymocyte Globulin in Treating Patients With Bone Marrow Failure Syndrome Status COMPLETED Phase PHASE2