NCT02530905 Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Patients Status COMPLETED Phase PHASE1
NCT02525302 HT-100 Long-term Study in DMD Patients Who Completed HALO-DMD-02 Status TERMINATED Phase PHASE2
NCT02516085 Improved Muscle Function in Duchenne Muscular Dystrophy Through L-Arginine and Metformin Status COMPLETED Phase PHASE1
NCT02500381 Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD) Status COMPLETED Phase PHASE3
NCT02485938 HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne) Status COMPLETED Phase PHASE2
NCT02484560 Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2 Status UNKNOWN Phase PHASE1
NCT02418338 2D Strain Evaluation: Children With Duchenne Muscular Dystrophy Versus Healthy Children Status COMPLETED Phase NA
NCT02376816 Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE1
NCT02354781 Clinical Intramuscular Gene Transfer of rAAV1.CMV.huFollistatin344 Trial to Patients With Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE1/PHASE2
NCT02354352 Therapeutic Potential for Aldosterone Inhibition in Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE3
NCT02340923 A Device for Rapid, Painless, Bedside Muscle Evaluation of Children Status COMPLETED Phase N/A
NCT02329769 Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD) Status TERMINATED Phase PHASE2
NCT02310763 A Phase 2 Study to Evaluate the Safety, Efficacy, Pharmacokinetics and Pharmacodynamics of PF-06252616 in Duchenne Muscular Dystrophy Status TERMINATED Phase PHASE2
NCT02295748 An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort Status COMPLETED Phase PHASE1
NCT02285673 Efficacy of Umbilical Cord Mesenchymal Stem Cells in Duchenne Muscular Dystrophy Status UNKNOWN Phase PHASE1/PHASE2
NCT02251600 A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy Status COMPLETED Phase PHASE1