Behavioral Effects of Kuvan in Children With Mild Phenylketonuria
- Status
- TERMINATED
- Phase
- N/A
Clinical Trials Related to BioMarin Pharmaceutical
Related studies linked through entity extraction aliases.
Oral 6R-BH4 for the Treatment of Isolated Systolic Hypertension and Endothelial Dysfunction
- Status
- TERMINATED
- Phase
- PHASE2
A Phase 1 Study to Evaluate Effects of Sapropterin Dihydrochloride on QTc Intervals in Healthy Adult Subjects
- Status
- COMPLETED
- Phase
- PHASE1
A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
- Status
- TERMINATED
- Phase
- N/A
PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry
- Status
- COMPLETED
- Phase
- N/A
Sapropterin in Individuals With Phenylketonuria
- Status
- COMPLETED
- Phase
- N/A
Study to Evaluate the Effects of Kuvan on Individuals With Phenylketonuria (PKU) With Maladaptive Behaviors
- Status
- COMPLETED
- Phase
- N/A
Nutritional and Neurotransmitter Changes in PKU Subjects on BH4
- Status
- COMPLETED
- Phase
- N/A
Safety and Tolerability Study of rAvPAL-PEG to Treat Phenylketonuria
- Status
- COMPLETED
- Phase
- PHASE1
Tetrahydrobiopterin in Patients With Chronic Kidney Disease (CKD) and Albuminuria
- Status
- COMPLETED
- Phase
- PHASE2
A Phase 2, Pharmacokinetic (PK) Study of 6R-BH4 Alone or 6R-BH4 With Vitamin C in Subjects With Endothelial Dysfunction
- Status
- COMPLETED
- Phase
- PHASE2
Sapropterin Expanded Access Program
- Status
- APPROVED_FOR_MARKETING
- Phase
- N/A
A Phase 2 Study of the Effects of 6R-BH4 in Subjects With Sickle Cell Disease
- Status
- COMPLETED
- Phase
- PHASE2
6R-BH4 Pulmonary Arterial Hypertension Study
- Status
- COMPLETED
- Phase
- PHASE1
Effect of 6R-BH4 Treatment in Coronary Artery Disease (OXBIO Study)
- Status
- UNKNOWN
- Phase
- PHASE2
A Phase 2 Study of the Effects of Sapropterin Dihydrochloride on Symptomatic Peripheral Arterial Disease
- Status
- COMPLETED
- Phase
- PHASE2
Safety and Efficacy Study of Phenoptin in Subjects With Hyperphenylalaninemia Due to BH4 Deficiency
- Status
- COMPLETED
- Phase
- PHASE2
Study of Phenoptin in Subjects With Phenylketonuria Who Participated in Protocols PKU-004 or PKU-006
- Status
- COMPLETED
- Phase
- PHASE3
A Study of the Effects of 6R-BH4 on Blood Pressure in Subjects With Poorly Controlled Systemic Hypertension
- Status
- COMPLETED
- Phase
- PHASE2
A Phase 4 Two Dose Level Study of Naglazyme(TM) (Galsulfase) in Infants With MPS VI
- Status
- COMPLETED
- Phase
- PHASE4