9 participants
Extension Study to Study PQ-110-001 (NCT03140969)
- Study Type:
- INTERVENTIONAL
- Last Updated:
- 2024-10-15
- Start Date:
- 2019-05-13
- Completion:
- 2022-10-03
Conditions
- Leber Congenital Amaurosis 10
- Blindness
- Leber Congenital Amaurosis
- Vision Disorders
- Sensation Disorders
- Neurologic Manifestations
- Eye Diseases
- Eye Diseases, Hereditary
- Eye Disorders Congenital
- Retinal Disease
Interventions
- DRUG