12 participants
A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)
- Study Type:
- INTERVENTIONAL
- Last Updated:
- 2020-07-30
- Start Date:
- 2014-12-31
- Completion:
- 2016-05-31
Conditions
- MPS 7
- Sly Syndrome
- Mucopolysaccharidosis
- MPS VII
Interventions
- DRUG
- OTHER