Congenital Hemolytic and Dyserythropoietic Anemias
NCT07649213 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 400
Last updated 2026-06-17
Summary
The main reason for this research study is to further understand how some red blood cells are formed incorrectly or they have an abnormal metabolism in a way that they break easier in the circulation or during their passage through the spleen.
Participants and/or family members diagnosed with non-immune hemolytic anemia due to a genetic disorder, such as, hemoglobin disorder, erythrocyte membrane skeleton disorders (e.g. spherocytosis, elliptocytosis, or stomatocytosis) or hydration defect (e.g. xerocytosis, overhydrocytosis) or red blood cell (RBC) enzyme disorders, or with a congenital dyserythropoietic anemia (CDA) will be asked to participate.
Conditions
- Hemolytic Anemia
Sponsors & Collaborators
-
Children's Hospital Medical Center, Cincinnati
lead OTHER
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2011-07-25
- Primary Completion
- 2050-07-31
- Completion
- 2052-07-31
Countries
- United States
Study Locations
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