A Study of the Natural Course of SURF1 Deficiency
NCT05277363 · Status: WITHDRAWN · Type: OBSERVATIONAL
Last updated 2022-05-20
Summary
The purpose of the study is to prospectively and systematically collect standardized clinical information, to describe important features of the disease course of SURF1 deficiency. These include but are not limited to symptomatology, clinical course, and risk factors for severe disease and complications.
Conditions
- Leigh Syndrome
Interventions
- OTHER
-
None (Observational study)
No investigational intervention, marketed product, or placebo will be administered to study participants in this study.
Sponsors & Collaborators
-
Taysha Gene Therapies, Inc.
lead INDUSTRY
Eligibility
- Max Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2022-05-04
- Primary Completion
- 2022-05-04
- Completion
- 2022-05-04
Countries
- United States
Study Locations
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