Defining Endpoints in Becker Muscular Dystrophy
NCT05257473 · Status: ACTIVE_NOT_RECRUITING · Type: OBSERVATIONAL · Enrollment: 80
Last updated 2025-06-08
Summary
This is a 24-month, observational study of 50 participants with Becker muscular dystrophy (BMD)
Conditions
- Becker Muscular Dystrophy
- Muscular Dystrophies
- Muscular Dystrophy in Children
- Muscular Dystrophy, Becker
Sponsors & Collaborators
-
Edgewise Therapeutics, Inc.
collaborator INDUSTRY -
Virginia Commonwealth University
lead OTHER
Principal Investigators
-
Nicholas E. Johnson, MD · Virginia Commonwealth University
Eligibility
- Min Age
- 6 Years
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2022-04-13
- Primary Completion
- 2026-05-31
- Completion
- 2026-05-31
Countries
- United States
- New Zealand
- United Kingdom
Study Locations
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