A Retrospective Study of Subjects With Thymidine Kinase 2 Deficiency
NCT05017818 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 61
Last updated 2023-09-01
Summary
This is a multicenter, multinational, retrospective chart-review study to evaluate survival in patients with Thymidine Kinase 2 deficiency (TK2d).
Conditions
- Thymidine Kinase 2 Deficiency
Interventions
- OTHER
-
Observational retrospective data
Non-intervention
Sponsors & Collaborators
-
Zogenix MDS, Inc.
lead INDUSTRY
Principal Investigators
-
UCB Cares, MD · 001 844 599 2273
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2021-07-23
- Primary Completion
- 2022-01-21
- Completion
- 2022-01-21
Countries
- United States
- Russia
- Spain
- Turkey (Türkiye)
Study Locations
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