High Risk Screen of Childhood Late-onset Pompe Disease in Pediatric Outpatient Clinics
NCT04981210 · Status: UNKNOWN · Type: OBSERVATIONAL · Enrollment: 1500
Last updated 2023-04-19
Summary
Establish of high-risk screening criteria to earlier identify possible childhood LOPD for early treatment and better prognosis. Therefore, validation of the high-risk screening criteria for childhood LOPD will be critical for identifying children of LOPD in Taiwan.
Conditions
- Pompe Disease
Sponsors & Collaborators
-
National Taiwan University Hospital
lead OTHER
Eligibility
- Min Age
- 1 Year
- Max Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2021-08-01
- Primary Completion
- 2023-07-31
- Completion
- 2024-07-31
Countries
- Taiwan
Study Locations
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