A Study to Assess Choroideremia (CHM) Health Outcomes
NCT04750785 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 46
Last updated 2021-10-14
Summary
The primary objectives of this study are to describe disease progression and severity by age in participants with CHM, to assess health-related quality-of-life, resource utilization and work productivity, and to assess quality-of-life, work productivity, and impact on daily activities in caregivers of participants with CHM at different stages of disease progression.
Conditions
- Choroideremia
Interventions
- OTHER
-
No Intervention
Administered as specified in the treatment arm.
Sponsors & Collaborators
- lead INDUSTRY
Principal Investigators
-
Medical Director · Biogen
Eligibility
- Sex
- MALE
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2020-12-15
- Primary Completion
- 2021-09-27
- Completion
- 2021-09-27
Countries
- United States
Study Locations
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