An Observational Study in Adult Patients With Non-dystrophic Myotonic Disorders
NCT04616807 · Status: ACTIVE_NOT_RECRUITING · Type: OBSERVATIONAL · Enrollment: 53
Last updated 2025-07-25
Summary
This is a non-interventional, prospective, observational, multicentre study to evaluate the long-term safety and effectiveness of Namuscla in adult patients with NDM.
Conditions
- Myotonic Dystrophy
Interventions
- DRUG
-
Mexiletine
Observational Study
Sponsors & Collaborators
-
Lupin Ltd.
lead INDUSTRY
Eligibility
- Min Age
- 18 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2020-12-17
- Primary Completion
- 2025-12-19
- Completion
- 2026-01-24
Countries
- France
- Germany
- United Kingdom
Study Locations
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