A Follow-up Study in Patients With Inherited Metabolic Disorders (IMD) Who Underwent Hematopoietic Stem Cell Transplantation (HSCT) With MGTA-456
NCT04008849 · Status: TERMINATED · Type: OBSERVATIONAL · Enrollment: 3
Last updated 2021-03-15
Summary
A follow-up study to evaluate the safety and clinical outcomes of patients with inherited metabolic disorders (IMD) who have undergone hematopoietic stem cell transplantation (HSCT) with MGTA-456
Conditions
- Inherited Metabolic Disorders (IMD)
Interventions
- OTHER
-
Safety and efficacy assessments
Long term safety and clinical outcomes
Sponsors & Collaborators
-
Magenta Therapeutics, Inc.
lead INDUSTRY
Principal Investigators
-
Paul J Orchard, MD · University of Minnesota
Eligibility
- Max Age
- 16 Years
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2019-05-21
- Primary Completion
- 2020-10-08
- Completion
- 2020-10-08
- FDA Drug
- Yes
Countries
- United States
Study Locations
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