MedTrace Logo

A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)

NCT03822650 · Status: COMPLETED · Type: OBSERVATIONAL · Enrollment: 37

Last updated 2024-06-27

No results posted yet for this study

Summary

CLN5 is a form of Batten Disease, a neurodegenerative disorder in children causing psychomotor regression, seizures, blindness, loss of ambulation and premature death, and has no available treatments.

The purpose of this study is to investigate the clinical characteristics and natural clinical progression of symptoms in individuals with CLN5. This natural history study is important to better understand disease course to be able to determine clinically relevant outcome measures for use in future clinical trials.

Conditions

  • Ceroid Lipofuscinosis, Neuronal 5

Sponsors & Collaborators

  • Neurogene Inc.

    lead INDUSTRY

Principal Investigators

  • Elise Beausoleil · Neurogene Inc.

Eligibility

Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

Start
2019-03-13
Primary Completion
2024-05-30
Completion
2024-05-30

Countries

  • United States

Study Locations

More Related Trials

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT03822650 on ClinicalTrials.gov