Study of Individuals Affected With Hypoplasminogenemia
NCT03797495 · Status: RECRUITING · Type: OBSERVATIONAL · Enrollment: 100
Last updated 2025-08-28
Summary
This is an Investigator initiated retrospective and prospective single cohort study. The study will utilize an international registry and develop a specimen biobank to provide an improved understanding of the natural history of hyposplasminogenemia, to elucidate the heterogeneity of phenotypic expression, identify markers to predict disease course, and inform improved therapeutic modalities
Conditions
- Plasminogen Deficiency
Sponsors & Collaborators
-
Fondazione Angelo Bianchi Bonomi
collaborator OTHER -
Indiana Hemophilia &Thrombosis Center, Inc.
lead OTHER
Principal Investigators
-
Amy D Shapiro, MD · Indiana Hemophilia &Thrombosis Center, Inc.
-
Flora Peyvandi, MD, PhD · Univeristy of Milan
Eligibility
- Sex
- ALL
- Healthy Volunteers
- No
Timeline & Regulatory
- Start
- 2018-12-18
- Primary Completion
- 2027-03-08
- Completion
- 2027-04-19
Countries
- United States
- Argentina
- Australia
- Austria
- Canada
- Greece
- Israel
- Italy
- Thailand
- Turkey (Türkiye)
- United Kingdom
Study Locations
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