Expanded Access to Triheptanoin

NCT03773770 · Status: AVAILABLE · Type: EXPANDED_ACCESS

Last updated 2026-04-13

No results posted yet for this study

Summary

Expanded access may be provided for qualified patients who have limited treatment options and are not eligible for a clinical trial.

Conditions

  • Long Chain Fatty Acid Oxidation Disorders

Interventions

DRUG

Triheptanoin

Liquid for oral (PO) or enteral tube administration

Sponsors & Collaborators

Principal Investigators

  • Medical Director · Ultragenyx Pharmaceutical Inc

Eligibility

Sex
ALL
Healthy Volunteers
No

Timeline & Regulatory

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Entities

Read the full study record

This page highlights key information. For complete eligibility criteria, study locations, investigator contacts, and the full protocol, visit the original record on ClinicalTrials.gov.

View NCT03773770 on ClinicalTrials.gov