Charcot-Marie-Tooth Disease (CMT) Infant Scale (INC-6611)

Summary

The purpose of this study is to develop and validate a clinical outcome measure to evaluate disability and disease progression of children 3 years of age and younger (infants and toddlers) with various types of Charcot-Marie-Tooth disease (CMT).

Conditions

• Charcot-Marie-Tooth Disease

Interventions

OTHER

No intervention involved

Sponsors & Collaborators

• University of Iowa

  collaborator OTHER

• Children's Hospital of Philadelphia

  collaborator OTHER

• University of Pennsylvania

  collaborator OTHER

• University of Rochester

  collaborator OTHER

• National Hospital of Neurology and Neurosurgery

  collaborator UNKNOWN

• Dubowitz Neuromuscular Centre

  collaborator OTHER

• University of Miami

  collaborator OTHER

• Carlo Besta Neurological Institute

  collaborator OTHER

• Johns Hopkins University

  collaborator OTHER

• Vanderbilt University

  collaborator OTHER

• University of Washington

  collaborator OTHER

• Nemours Children's Hospital

  collaborator OTHER

• National Institutes of Health (NIH)

  collaborator NIH

• Stanford University

  collaborator OTHER

• Cedars-Sinai Medical Center

  collaborator OTHER

• Harvard/Massachusetts General Hospital

  collaborator UNKNOWN

• University of Michigan

  collaborator OTHER

• University of Minnesota

  collaborator OTHER

• University of Utah

  collaborator OTHER

• University of Connecticut

  collaborator OTHER

• Universiteit Antwerpen

  collaborator OTHER

• Sydney Children's Hospitals Network

  lead OTHER

Eligibility

Max Age

4 Years

Sex

ALL

Healthy Volunteers

Yes

Timeline & Regulatory

Start

2016-10-31

Primary Completion

2017-12-31

Countries

• United States
• Australia
• Italy

Study Locations